Building a New Future: Our Family’s Floor Plans to a New Accessible Home
As mobility decreases, typical houses may become inaccessible for people with Duchenne. JeanAnn Bryan shares how she and her family built a new home that was accessible for her two […]
Cure Rare Disease – 3 Years Later
In the three years since the founding of Cure Rare Disease, there have been many accomplishments on our journey to creating the first custom drug therapy for rare disease patients. […]
My Child in Disguise
Though steroids can slow the progression of Duchenne, they come with a variety of difficult side effects. Sara Aluffi talks about the varying emotions that come with watching her son […]
Findings From Cure Rare Disease’s AAV Seropositivity Study
In 2020, we launched our study into our patient’s AAV neutralizing antibodies, a key factor in how effective certain gene therapies may be for them. A year after the start […]
A Timeline Of The Science Behind Cure Rare Disease
Cure Rare Disease would not be where it is today without the work of previous scientists in developing CRISPR technology. As we approach the dosing of our first patient, learn […]
Postural Orthostatic Tachycardia Syndrome (POTS)
CRD intern Katie Kuhl shares her daily life with Postural Orthostatic Tachycardia Syndrome on POTS Awareness Day.